The FDA granted fast track designation for CTx001, an investigational gene therapy candidate for geographic atrophy secondary ...
What is IZERVAY™?IZERVAY (avacincaptad pegol intravitreal solution) is a prescription eye injection, used to treat geographic atrophy (GA), the advanced form of dry age-related macular degeneration ...
Injections for spinal muscular atrophy (SMA) refer to two treatments that the Food and Drug Administration (FDA) has approved for SMA: nusinersen (Spinraza) and onasemnogene abeparovec-xioi (Zolgensma ...
11don MSN
What is spinal muscular atrophy type 1 as Jesy Nelson's twins receive heartbreaking diagnosis
Singer Jesy Nelson has opened up sharing that her twin daughters have been diagnosed with Spinal Muscular Atrophy, but what ...
Panelists discuss how spinal muscular atrophy is an autosomal recessive genetic disease affecting motor neurons with 3 currently approved disease-modifying therapies that restore SMN protein ...
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