UCLA researchers have developed a lipid nanoparticle-based gene-editing approach capable of inserting an entire healthy gene ...

UCLA researchers have developed a lipid nanoparticle-based gene-editing approach capable of inserting an entire healthy gene into human airway cells, restoring key biological function in a laboratory ...

Boehringer Ingelheim is discarding an inhaled gene therapy designed to treat cystic fibrosis (CF) after terminating a phase 1 ...

Experts in cloning and stem cell science are reporting that five lung stem cell variants dominate the lungs of patients with advanced cystic fibrosis, and that these variants drive key aspects of CF ...

Cystic fibrosis (CF) is the most common inherited metabolic disease in Europe. More than 8,000 people in Germany are affected ...

The mucus in the airways is not as sticky, inflammation in the lungs significantly reduced: Triple combination therapy can achieve these positive, lasting effects in patients with cystic fibrosis (CF) ...

Cystic fibrosis (CF) is a disease that people can be born with. While there is no cure, people with CF may live well into adulthood if they receive the appropriate treatment and medical monitoring.

The development of gene editing tools, which enable the specific targeting and correction of mutations, hold the promise of allowing us to correct those mutations that cause genetic diseases. However, ...

CLEVELAND, Ohio — Many patients with advanced cystic fibrosis — an illness that causes thick mucus secretions — turn to lung transplants to improve their quality of life. But in taking that step, they ...

PHILADELPHIA (CBS) -- A desperate fight for life for a young woman in Montgomery County. She needs a lung transplant but has been rejected by most hospitals. Follow the tubing to 22-year-old Jen ...