Glycogen storage diseases (GSDs) constitute a group of inherited metabolic disorders that impair normal glycogen synthesis or degradation, resulting in the accumulation of structurally abnormal ...
CALIFORNIA -- ABC News reported a tale of two friends, one on a mission to help the other battling a rare disease. The two, Dylan Siegel and his best friend Jonah Pournazarian have reached a ...
Ultragenyx is gearing up to take its glycogen storage disease (GSD) treatment to regulators next year after the gene therapy helped patients reduce their intake of cornstarch, which is currently used ...
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