Bayer's pioneering cell and gene therapies for Parkinson's disease are at the forefront of an exciting but risky test of CEO ...

At the European Cell & Gene Therapy Summit 2025, funding challenges and innovation drove discussions on the sector’s future.

Three draft recommendation documents published on Wednesday are intended to guide drug sponsors and accelerate the ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the ...

Exagamglogene autotemcel (exa-cel), a CRISPR/Cas9 gene-edited cell therapy, eliminated vaso-occlusive crises in 97% of ...

September is Sickle Cell Awareness Month, and millions of people worldwide are living with the disease. But advances in ...

A one-time experimental treatment shows unprecedented success in slowing Huntington's disease, according to UCL researchers.

Being proactive — especially when it comes to testing, process development and preparing for commercialization — can greatly decrease the risk that your CGT will receive a CRL.

The American Society of Health-System Pharmacists has launched the  ASHP Center for Next Generation Therapeutics, aimed at supporting hospitals and ...

ProBio recently opened a gene therapy hub in a 128,000-square-foot facility in Mercer County, bringing more than 100 ...

SynGenSys, a biotechnology company designing synthetic gene promoter systems to address critical bottlenecks in biopharma ...

Researchers at the University of Oslo and Oslo University Hospital have developed a promising new immunotherapy targeting the ...