What Is Sephience, and Why Does It Matter? Sephience (sepiapterin) is a new oral medication approved by the FDA to treat a rare inherited condition known as phenylketonuria (PKU) in adults and ...
Following a low-phenylalanine diet can prevent intellectual disability and other complications in people with phenylketonuria. The diet focuses on low protein foods and avoids high protein foods.
People with phenylketonuria cannot break down a substance in food called phenylalanine. Following a phenylketonuria diet is the main treatment for preventing serious symptoms. People with ...
Biotech firm PTC Therapeutics said Wednesday that its drug for phenylketonuria, or PKU, met its key goal in a Phase 3 study. In PKU, patients’ bodies are unable to break down the amino acid ...
Credit: Getty Images. The Company has initiated a phase 3 study, Synpheny-3. The Food and Drug Administration (FDA) has granted Fast Track designation to Synlogic’s labafenogene marselecobac for the ...
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BioMarin Pharmaceutical Inc.’s (BMRN) Phenylketonuria Candidate Drug Impresses in Phase 3 Trials
BioMarin Pharmaceutical Inc. (NASDAQ: BMRN) is one of the best beginner stocks to buy, according to analysts. On September 6, ...
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