News

Roche (SIX:ROG) shares dropped 2% on Monday after the company paused dosing of its gene therapy Elevidys in non-ambulatory ...
Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today provided a safety ...
Participants with Duchenne muscular dystrophy (DMD) who received RGX-202 demonstrated functional improvement and better ...
The drug, Givinostat, has been approved as safe for use but Belfast Health Trust, NI's specialist centre for the condition, ...
Parents of children with an incurable muscle-wasting condition have called on the Minister for Health to accelerate the ...
Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies ...
U.S. FDA successfully completed Pre-License Inspection; Company expects facility will meet all requirements to support ...
The parents of a nine-year-old boy battling a devastating muscle-wasting condition say new research could offer them more ...
The campaign to commemorate the work of the Muscular Dystrophy Association was created in partnership with agency Yes&.