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Zevra Therapeutics embarks on diagnosis push as Miplyffa launch gains steam
It’s been just six months since Zevra Therapeutics scored an FD | Niemann-Pick disease type C therapy Miplyffa became ...
How Gene Hackman’s dogs helped first responders find actor’s dead body after searching for 30 minutes
The emergency medical responders initially thought one of the dogs wanted to play, but they quickly realized it was trying to lead them somewhere.
Threat to son's treatment for rare disease 'agony'
A mother has spoken about her "painful" experience over the potential end to her son's life-enhancing treatment for a rare ...
Bruce Willis’s wife issues statement after deaths of Gene Hackman and Betsy Arakawa: ‘Caregivers need care, too’
His wife, as well as his daughters and ex-wife Demi Moore, have been praised for their candour discussing his condition, and ...
Trump administration live updates: Trump, NATO leader to meet at White House
President Donald Trump is scheduled Thursday to welcome NATO Secretary General Mark Rutte to the White House. The pair are ...
Quoin Pharmaceuticals, Inc.: Quoin Pharmaceuticals Provides Corporate Update and Reports Fourth Quarter and Full-Year 2024 Financial Results
Quoin Pharmaceuticals Ltd. (NASDAQ: QNRX) (the "Company" or "Quoin"), a late clinical-stage specialty pharmaceutical company focused on rare and orphan ...
Prince Frederik of Luxembourg’s final days: Filmmaker recalls 22-year-old's battle with rare disease
Two weeks after Prince Frederik of Luxembourg died from POLG, a documentary filmmaker has revealed that the 22-year-old struggled to "get up by himself" as he battled the rare genetic disorder in an ...
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Gene Hackman Case: How Surviving Dogs Helped Paramedics Find His Body
After paramedics found Gene Hackman’s wife Betsy Arakawa dead in the bathroom of their Santa Fe home, the couple’s dogs led authorities to the actor’s body.
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Q&A: ‘An exciting breakthrough’: Gene transfer therapy promising in Danon disease
Danon disease is a rare but serious cardiomyopathy that drastically reduces life expectancy. Male patients infrequently live ...
Polar Plunge in honor of Staten Islander with rare skin disease planned for this month
STATEN ISLAND, N.Y. — A fundraising Polar Plunge to honor John Hudson Dilgen will take place this month in South Beach to ...
How to care for a loved one with dementia: 5 expert tips
About 7 million Americans have Alzheimer’s, and their family members often help care for them as the disease progresses. Here are five tips if you become a caregiver for someone with dementia.
Director Who Worked With Prince Frederik Says it Was ‘Painful’ to Watch Him Struggle Before His Death
Filmmaker Mei Fa Tan reflected on her experience working with Luxembourg’s Prince Frederik before his death at the age of 22.